The world's most expensive drugs

Genzyme drugs take four spots among the most expensive in a Forbes survey (chart). The developer's rare disease treatments Myozyme, Fabrazyme, Cerezyme and Aldurazyme all cost over $200,000 per year. But the Cerezyme price is likely to head south following last week's FDA approval of Shire's Gaucher treatment, velaglucerase alfa for injection. Alexion Pharmaceuticals takes the top spot for the world's most expensive drug, Soliris. The therapy costs $409,500 per year. Chart | Article | Genzyme release


Using AI and RWD to Uncover Rare Disease Insights, Accelerate Commercialization and Improve Patient Outcomes

Wednesday, March 24 | 2pm ET / 11am PT

Learn how transformed real world data into real world insights to assist Audentes in their development of AT132 for the treatment of XLMTM. The session reviews how IPM.ia and Audentes collaborated to uncover the XLMTM patient population.