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Niemann-Pick type C disease
Pharma
Zevra embarks on diagnosis push as Miplyffa launch gains steam
The company estimates there are around 900 patients with Niemann-Pick disease type C in the U.S.
Zoey Becker
Mar 13, 2025 11:24am
Zevra lines up $150M from sale of PRV tied to Miplyffa approval
Feb 27, 2025 9:58am
Zevra pegs Miplyffa as 'cornerstone' of Niemann-Pick treatment
Oct 4, 2024 6:45am
IntraBio hits the ground running with new rare disease launch
Sep 30, 2024 3:25pm
IntraBio snags FDA nod in rare disease just days after Zevra
Sep 25, 2024 9:50am
Zevra snags FDA approval for new lysosomal storage disorder med
Sep 20, 2024 1:54pm
