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genetic diseases

FDA
Pharma

FDA approves Soleno's Vykat XR for insatiable hunger disorder

The FDA has approved Soleno Therapeutics' Vykat XR as the first treatment for insatiable hunger related to the rare condition Prader-Willi Syndrome.
Kevin Dunleavy Mar 27, 2025 11:24am
Ionis headquarters

Tryngolza's FDA approval marks 'pivotal moment' for Ionis: CEO

Dec 20, 2024 8:32am
Alnylam Family Health History Road Trip Bernice Bennett

Alnylam embarks on campaign to drive hATTR amyloidosis diagnoses

Mar 13, 2024 10:30am
Novartis building

Pharming scores FDA nod for rare disease drug Joenja

Mar 27, 2023 11:06am

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