gene therapy

FDA

Pharma

FDA probes Novartis’ Zolgensma gene therapy over cancer risks

The FDA also flagged two recent reports of other gene therapy candidates where AAV vector integration drove tumor formation.

Angus Liu Nov 9, 2026 11:14am

NVS

Novartis confirms several new tumor cases in Zolgensma patients

Nov 6, 2026 9:59am

sale transaction MA deal changing hands money money changing hands

Ultragenyx cashes in a pair of FDA review vouchers for $413M

Oct 14, 2026 4:19pm

Sunrise over foggy forest in Tuscany Italy

FDA approves Ultragenyx gene therapy after prior rejection

Sep 17, 2026 4:50pm

globe asia

China IIT, Daiichi Sankyo-AZ, Leo-Tanabe—Fierce Pharma Asia

Aug 21, 2026 9:00am

An artists impression of DNA The DNA appears to be made up of glowing orbs and appears on a blue background

Ultragenyx, after FDA speed bump, lands 1st gene therapy nod

Aug 19, 2026 10:33pm