Keyword: Exondys 51

Sarepta’s new CEO pick, Doug Ingram, wins plaudits for commercial savvy, CNS expertise—and sets the stage for more M&A chatter.

Should drugs that win conditional FDA approval command the same high prices as products that undergo the full menu of agency scrutiny?

PTC says it'll charge $35,000 for Emflaza, the Duchenne drug it bought from Marathon in March, amid a brouhaha over its $89,000 list price. Is the new sticker low enough?

You know that old saw about every med school graduate winning the “Doctor” title? Something similar could apply to Sarepta’s newly approved Duchenne muscular dystrophy med Exondys 51.